Mucopolysaccharidosis VI
Showing 1 - 25 of 432
Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Torrance (Adalimumab Injection [Humira],
Recruiting
- Mucopolysaccharidosis I
- +2 more
- Adalimumab Injection [Humira]
- Saline Solution for Injection
-
Torrance, CaliforniaThe Lundquist Institute at Harbor-UCLA Medical Center
Aug 9, 2022
Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis IV A Trial in San Francisco (There is no intervention)
Recruiting
- Mucopolysaccharidosis I
- +7 more
- There is no intervention
-
San Francisco, CaliforniaUniversity of California San Francisco
Nov 9, 2022
MPS (RaDiCo Cohort) (RaDiCo-MPS)
Recruiting
- Mucopolysaccharidosis I
- +7 more
-
Angers, France
- +22 more
Sep 12, 2023
Mucopolysaccharidosis Type VI Trial in Naples, Ankara (AAV2/8.TBG.hARSB)
Active, not recruiting
- Mucopolysaccharidosis Type VI
- AAV2/8.TBG.hARSB
-
Naples, Italy
- +1 more
Nov 22, 2021
Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human
Completed
- Mucopolysaccharidosis I
- +15 more
- Human Placental Derived Stem Cell
-
Denver, Colorado
- +2 more
Oct 24, 2022
MPS IVA, MPS VI Trial in Oakland (Vosoritide Injection [Voxzogo])
Not yet recruiting
- MPS IVA
- MPS VI
- Vosoritide Injection [Voxzogo]
-
Oakland, CaliforniaUCSF Benioff Children's Hospital Oakland
May 4, 2023
ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn
Enrolling by invitation
- Acid Sphingomyelinase Deficiency
- +13 more
- Confirmatory Testing
-
Bronx, New York
- +9 more
May 9, 2022
Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD
Recruiting
- Mucopolysaccharidosis Disorders
- +28 more
- Stem Cell Transplantation
- +7 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Nov 1, 2022
Baby Detect : Genomic Newborn Screening
Recruiting
- Congenital Adrenal Hyperplasia
- +126 more
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Jan 24, 2023
Mucopolysaccharidosis IV A, Mucopolysaccharidosis VI, Mucopolysaccharidoses Trial in Porto Alegre (Losartan, Placebo)
Recruiting
- Mucopolysaccharidosis IV A
- +8 more
- Losartan
- Placebo
-
Porto Alegre, Rio Grande Do Sul, BrazilHospital de Clinicas de Porto Alegre
Oct 2, 2020
Maroteaux-Lamy Syndrome Trial in Minneapolis (Naglazyme®)
Terminated
- Maroteaux-Lamy Syndrome
-
Minneapolis, MinnesotaUniversity of Minnesota Medical Center, Fairview
Dec 22, 2020
Biomarker for Maroteaux-Lamy Disease (BioMaroteaux)
Active, not recruiting
- Lysosomal Storage Disease
- +4 more
-
Cairo, Egypt
- +4 more
May 17, 2021
Mucopolysaccharidosis VI Clinical Surveillance Program
Completed
- Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome)
-
Irvine, California
- +49 more
Apr 2, 2021
Mucopolysaccharidosis I, II, and VI Screening inHigh-Risk
Terminated
- Mucopolysaccharidosis (MPS)
-
Los Angeles, California
- +13 more
Mar 16, 2021
Brain Structure and Function in MPS Disorders
Completed
- Mucopolysaccharidosis Type I
- +4 more
-
Oakland, California
- +3 more
Sep 4, 2019
Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Minneapolis (Somatropin (DNA origin))
Terminated
- Mucopolysaccharidosis I
- +2 more
- Somatropin (DNA origin)
-
Minneapolis, MinnesotaUniversity of Minnesota
Aug 6, 2018
MPS I, MPS II, MPS IVA Trial in San Francisco (Aldurazyme (laronidase))
Recruiting
- MPS I
- +8 more
- Aldurazyme (laronidase)
-
San Francisco, CaliforniaUniversity of California
Apr 21, 2022
Mucopolysaccharidosis IH/S, Mucopolysaccharidosis IS Trial in Minneapolis (Autologous Plasmablasts (B cells))
Not yet recruiting
- Mucopolysaccharidosis IH/S
- Mucopolysaccharidosis IS
- Autologous Plasmablasts (B cells)
-
Minneapolis, MinnesotaUniversity of Minnesota
Jan 20, 2023
Skin Laxity; Facial, Dry Skin; Facial Trial (HydraFacial Syndeo System, ReGen-GF)
Not yet recruiting
- Skin Laxity; Facial
- Dry Skin; Facial
- HydraFacial Syndeo System
- ReGen-GF
- (no location specified)
Jun 27, 2023
Before and After Hematopoietic Cell Transplantation in
Enrolling by invitation
- Hematopoietic Cell Transplantation
- Mucopolysaccharidosis Type I
- Laronidase therapy and a stem cell transplant
-
Minneapolis, MinnesotaUniversity of Minnesota Masonic Cancer Center
Nov 22, 2022
Glycogen Storage Disease VI, GLYCOGEN STORAGE DISEASE IXa1, GLYCOGEN STORAGE DISEASE IXa2 Trial in Durham (No intervention)
Recruiting
- Glycogen Storage Disease VI
- +4 more
- No intervention
-
Durham, North CarolinaDuke University
Jul 27, 2022
Mucopolysaccharidosis Type II Observational
Withdrawn
- Mucopolysaccharidosis II
- Observational
-
Oakland, California
- +2 more
Oct 6, 2022